Kiran Musunuru

Company: University of Pennsylvania

Job title: Professor

Seminars:

Morning Workshop: Expanding Rare Disease Targeting Using Lessons Learned from Baby KJ’s Personalized CRISPR Therapy 9:30 am

Following the groundbreaking work to launch the world's first personalized CRISPR therapy to treat baby KJ, a new blueprint for rare disease treatment is forming. This interactive workshop with the baby KJ team offers unmissable insights into how this pioneering approach to precision medicine has created a transformative model for targeting rare diseases more effectively…Read more

day: Day Two

The Future: How Baby KJ’s Personalized CRISPR Therapy Will Facilitate Better Rare Disease Targeting 9:35 am

Following the groundbreaking work to launch the world’s first personalized CRISPR therapy to treat baby KJ, a new blueprint for rare disease treatment is forming. With the baby KJ team swiftly adapting base editing technology, rapidly co-ordinating regulatory approval and redefining clinical strategies, this session offers an unmissable insight into how this pioneering approach to…Read more

day: Pre-Conference Workshop Day