Promoting How Gene Editing Has Fast-Tracked Novel Therapies for Complement-Driven Diseases
Time: 8:30 am
day: Day Two
Details:
- Explore the rationale behind developing gene therapy strategies including durability and convenience
- Understand the strategies available to develop gene therapies ranging from AAVmediated gene editing, first to third generation CRISPR gene editing therapies and epigenetic editors
- Emphasize how compared to these other available gene therapy strategies, why base editing technology is important and how base editing strategies have been guided through working in a collaboration with Beam Therapeutics
